Senate H.E.L.P. Committee Hearing: Treating Rare and Neglected Pediatric Diseases

Senate Committee on Health, Education, Labor, and Pensions (HELP),  Full Committee Hearing – Treating Rare and Neglected Pediatric Diseases: Promoting the Development of New Treatments and Cures

Click Here to Watch the Video of the Hearing


Panel I

  • Dr. Jesse Goodman , Chief Scientist, U.S. Food and Drug Administration, Silver Spring, MD
  • Dr. Alan Guttmacher , Acting Director, National Institute of Child Health and Human Development, Bethesda, MD

Panel II

  • Mr. Alex Silver , Founder, Jackson Gabriel Silver Foundation, New York, NY
  • Mr. John F. Crowley , President and CEO, Amicus Therapeutics, Cranbury, NJ
  • Ms. Diane Edquist Dorman , Vice President for Public Policy, National Organization for Rare Disorders, Washington, DC
  • Ms. Suerie Moon , Board Member, Doctors Without Borders USA, New York, NY
  • Dr. Daniel Frattarelli , Chair of Committee on Drugs, American Academy of Pediatrics, Dearborn, MI